A Look Into Everlume Bio
Drug Pipeline
Customer Driven Programs
Causative Gene
Disease
Bain Syndrome
MCOPS12
Laminin related MD
LMNA-related cardiac diseases
Hereditary Spastic Paraplegia
Sanfilippo Syndrome - Type B.
HMERF-Hereditary Myopathy with Early Respiratory Failure
GRIA Disorder
GRIN2B-related neurodevelopmental disorder
HSPB8 Myopathy
F-Box Only 31
Hereditary Spastic Paraplegia
Hereditary Spastic Paraplegia
Internal Programs
DIPG
Hereditary Spastic Paraplegia
HNRNPH2
RARB
LMNA
LMNA-Cardiac
SPG11
NAGLU
TTN
GRIA1
GRIN2B
HSPB8
FBXO31
SPG4
SPG7
SPG15
Pre-Clinical
IND Enabeling
Phase 1/2
A Look Into Everlume Bio
Drug Pipeline
It’s Time to Take Action
Time is life—every second counts in curing rare diseases.
Let’s take the first step together. We are on a mission to eliminate rare disease by 2035. We would love for you to join us.